Mark A. Kay, MD, PhD

Scientific Advisor

Dr. Kay is the Dennis Farrey Family Professor in the Departments of Pediatrics and Genetics, and Head of the Division of Human Gene Therapy in Pediatrics at the Stanford University School of Medicine. Before joining Stanford, Dr. Kay was an assistant/associate professor at the University of Washington in the Department of Medicine from 1993-1998. He has been a true bench-to-bedside physician-scientist – leading the first demonstration of therapeutic rAAV transduction of the liver in small and large animal models, working out the molecular process of AAV transduction in vivo, and playing a major role in developing a clinical trial representing the first systemic delivery of rAAV in humans.

Dr. Kay is one of the founders of the American Society of Gene Therapy and served as the President in 2005-2006. He has organized many national and international conferences including the first Gordon Conference related to gene therapy. He was elected to the American Academy of Pediatrics in 2010. In 2020 he was elected to the National Academy of Inventors.

Dr. Kay received his Medical Degree and PhD from Case Western Reserve University and completed a residency in pediatrics a fellowship in medical genetics and inborn errors of metabolism, and his postdoctoral research at Baylor College of Medicine.